Gene Therapy Advances in SCD and B-Thalassemia (with Dr Stefano Rivella)
Explore the latest breakthroughs in gene therapy for sickle cell disease and beta thalassemia with Dr. Stefano Rivella, hematologist and research faculty at Children's Hospital of Philadelphia.
In this episode, Dr. Rivella discusses the science behind FDA-approved therapies, compares gene addition and gene editing approaches, and shares insights on clinical safety, efficacy, and future innovations like in vivo gene therapy.
Learn about the challenges of access, cost, and global equity, and discover how evolving technologies could transform treatment for patients worldwide.
Host: Isabel…
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