Life with rare, incurable disease is all about quality
One in ten Americans, or one on every elevator and four on every bus, is impacted by a rare disease.
Yet, 95 percent of rare diseases do not have approved treatment. On a promising note, bio-pharmaceutical companies working on orphan drugs have more than 800 projects in clinical development.
In a ground-breaking clinical trial, a participating patient at the University of Connecticut Health Center was the first in the world to receive an infusion treatment for a type of glycogen storage disease.
This hour on Where We Live, we hear from the National Organization for Rare Disorders (NORD) on…
The skinny
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