Latest / Weekly Neurology Deep Dive - A review of recent impactful publications in the field of Neurology
Outcome Measures for Adult Becker Muscular Dystrophy Progression
This article is an excerpt from a natural history study published in Neurology in 2025, focusing on the sensitivity of clinical outcome measures in assessing adult patients with Becker Muscular Dystrophy (BMD) over a three-year period. Researchers aimed to identify which functional tests, such as the Rise From Floor velocity (RFFv) and the North Star Ambulatory Assessment (NSAA), were most responsive to the disease's slow and variable progression for use in clinical trials. The study concluded that RFFv was the only measure with high responsiveness across the entire cohort at three years…
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