Pegzilarginase: Accelerated Approval For Arginase 1 Deficiency (ARG1-D) Hyperargininemia
Pegzilarginase, first disease-modifying therapy for Arginase 1 deficiency, lowers toxic arginine levels, slows neurological damage, and transforms care through enzyme replacement, accelerated approval, and multidisciplinary support.
The skinny
The skinny isn't ready yet — notes appear once the transcript is processed.